Urea cycle disorders are a group of inherited metabolic disorders that make it difficult for patients to remove toxic waste products. The Food and Drug Administration (FDA) has granted Orphan Drug ...

Nitrogen is a big part of the air we breathe, but too much can kill. Researchers at Johns Hopkins University reviewed 25 years of studies on using sodium phenylacetate and sodium benzoate to help ...

Satellite Biosciences, Inc. (Satellite Bio), a biotechnology company developing off-the-shelf liver therapies designed to restore liver function in patients with severe liver diseases, today announced ...

An international research consortium co-led by Andrea L. Gropman, M.D., at Children's National Hospital has received $5 million in federal funding as part of an overall effort to better understand ...

Intravenous infusions of urea now appear to promise successful treatment of sickle-cell patients.… Urea causes sickled cells to revert to their normal, doughnut shape. Thus far, intravenous infusions ...

UCDs are devastating, life-threatening conditions with high infant mortality and significant risk of neurological injury, with no curative treatment available in the first weeks of life NEWTON, Mass.- ...