Fewer serious complications. Fewer hospitalizations and blood transfusions. Better growth and development. And a markedly ...

Families from across the nation gathered in Washington, D.C. this week to advocate for children's health care.

ORANGE, Ohio — An 8-year-old girl living with sickle cell anemia becomes a crime-fighting hero who rides a rainbow unicorn. A ...

June 2 (Reuters) - Shares of Fulcrum Therapeutics plunged 50% in premarket trading on Tuesday after the company said it would ...

Fewer serious complications. Fewer hospitalizations and blood transfusions. Better growth and development. And a markedly lower risk of death from the complications of sickle cell anemia. These are ...

Talazoparib plus enzalutamide reduces progression risk by 50% in men with DNA repair alter ...

A Silver Spring woman says for the first time in years, she’s feeling hopeful thanks to a groundbreaking therapy that’s ...

The study showed that an experimental pill from the company Revolution Medicines almost doubled metastatic pancreatic cancer patients’ survival times compared with chemotherapy.

Agios gains global rights to cevidoplenib for ITP, adding a late-stage rare hematology asset with up to $1B U.S. peak sales ...

(Correctseq), a clinical-stage biotechnology company pioneering transformer Base Editing (tBE) technology for severe diseases ...

But phase III study testing selinexor plus ruxolitinib splits on its main goals ...

Decision follows FDA feedback regarding the implications of the secondary malignancies observed with Tazverik®(tazemetostat) and the product’s subsequent global withdrawal on the benefit-risk profile ...