Dosing has begun in a Phase 2 clinical trial testing the experimental oral therapy SAT-3247 in boys with Duchenne muscular ...
Columnist Shalom Lim has discovered that a personal sense of belonging is built through simple presence. Art can help foster ...
Guest writer Matthew Busch says that, despite the setbacks and surgeries he's endured, he's now thriving in life with Duchenne MD.
Lasting gains in swallowing ability have been reported for four people with oculopharyngeal muscular dystrophy given gene therapy in a trial.